Why This Drug for Rare Metabolic Conditions Is Changing Genetics Medicine
A single infant, known publicly as KJ, is the reason genetic medicine will never be the same. Born with carbamoyl phosphate synthetase 1 deficiency — an...
Category Genetics
The Drug Reducing Death Risk After Acute MI by 25 Percent
Beta-blockers — a class of drugs that includes carvedilol, metoprolol, and bisoprolol — reduce the combined risk of death, recurrent heart attack, and...
The Drug That Halves Risk of Pancreatitis After ERCP Procedure
Rectal indomethacin, a common and inexpensive nonsteroidal anti-inflammatory drug, can cut the risk of pancreatitis after an ERCP procedure nearly in half.
Why Some Patients Are Getting DNA Tests Before Starting Antidepressants
Some patients are now getting DNA tests before starting antidepressants because roughly 60 percent of people with depression do not benefit from the first...
New Drug for Hereditary Transthyretin Polyneuropathy Works Without Surgery
For decades, the only meaningful treatment for hereditary transthyretin polyneuropathy was a liver transplant — a major surgical procedure that carried...
The Drug That Lowers the Risk of Preeclampsia in Pregnant Women
Low-dose aspirin, one of the cheapest and most widely available medications on the planet, is the drug that lowers the risk of preeclampsia in pregnant...
The Gene Silencing Drug Given Just Once for a Lifelong Condition
The gene silencing drug making headlines for its potential to treat a lifelong neurological condition with a single dose is called an RNA interference...
New Injectable for Hemophilia A Eliminates Daily Factor Replacement
A new class of injectable therapies for hemophilia A has fundamentally changed what it means to live with the condition, replacing the grueling routine of...
Why Some Cancer Drugs Now Come With Genetic Testing Requirements
Some cancer drugs now come with genetic testing requirements because certain patients carry gene variants that cause their bodies to metabolize these...
The Drug Approved for Rare Genetic Condition Benefiting Thousands
On March 10, 2026, the FDA approved Wellcovorin (leucovorin calcium) tablets as the first-ever treatment for cerebral folate transport deficiency caused...